5No authors listed. Help is Available for Patients Suffering from Rare Diseases; More Than 300 Orphan Drugs in Development Pipeline[N]. US Fed News Service, Including US State News. 2008-01-24.
6Carla Maria Teixeira de Barros, Ana Luisa Papoila. Therapeutic profile of orphan medicines[J]. Pharmacoepidemiology and Drug Safety, 2007,16 (4) : 435-440.