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用于治疗纯合子型家族性高胆固醇血症的药物Lomitapide 被引量:1
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作者 杨臻峥 《药学进展》 CAS 2013年第1期F0003-F0003,共1页
Aegerion制药公司开发的lomitapide(Juxtapid)于2012年12月21日获美国FDA批准,用于纯合子型家族性高胆固醇血症(HoFH)患者。
关键词 lomitapide Juxtapid 纯合子型家族性高胆固醇血症
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Unlocking the therapeutic potential of RNA splicing in lung fibrosis:Insights from the SRSF7-PKM axis
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作者 Bi-Sen Ding 《Acta Pharmaceutica Sinica B》 2025年第6期3351-3352,共2页
Breathing,an essential physiological process,enables the continuous exchange of gases necessary for maintaining internal metabolic balance.On average,an adult inhales and exhales roughly 10,000 to 12,000 L of air each... Breathing,an essential physiological process,enables the continuous exchange of gases necessary for maintaining internal metabolic balance.On average,an adult inhales and exhales roughly 10,000 to 12,000 L of air each day to sustain adequate oxygen levels1.The lungs,which serve as the body’s primary organs for gas exchange,possess a remarkable intrinsic capacity for self-repair and regeneration following injury2,3. 展开更多
关键词 Lung fibrosis Alternative splicing SRSF7 PKM exon skipping Fibroblast activation lomitapide
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